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SMN2 Gene Splicing Modifiers Restore Lifespan and Motor Behavior in a Mouse Model of Spinal Muscular Atrophy.
SMN2 Gene Splicing Modifiers Restore Lifespan and Motor Behavior in a Mouse Model of Spinal Muscular Atrophy.
2014
Nikolai A. Naryshkin
Marla Weetall
Amal Dakka
Jana Narasimhan
Xin Zhao
Zhihua Feng
Karen K. Y. Ling
Gary Mitchell Karp
Hongyan Qi
Matthew G. Woll
Guangming Chen
Nanjing Zhang
Vijayalakshmi Gabbeta
Priya Vazirani
Anuradha Bhattacharyya
Bansri S. Furia
Nicole Risher
Josephine Sheedy
Ronald Kong
Jiyuan
Jiyuan Ma
Anthony Turpoff
Chang-Sun Lee
Xiaoyan Zhang
Young-Choon Moon
Panayiota Trifillis
Ellen Welch
Joseph M. Colacino
John Babiak
Neil Gregory Almstead
Stuart W. Peltz
Loren A. Eng
Karen S. Chen
Jesse L. Mull
Maureen S. Lynes
Lee L. Rubin
Paulo Fontoura
Luca Santarelli
Daniel Haehnke
Kathleen McCarthy
Roland Schmucki
Martin Ebeling
Manaswini Sivaramakrishnan
Chien-Ping Ko
Sergey Paushkin
Hasane Ratni
Irene Gerlach
Anirvan Ghosh
Friedrich Metzger
Keywords:
Spinal muscular atrophy
Gene splicing
Neuroscience
Biology
motor behavior
Correction
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