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Rafael Ruiz de Assin
Rafael Ruiz de Assin
University of California, Los Angeles
Genetic enhancement
Hematopoietic stem cell
CD34
Stem cell
Haematopoiesis
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Preclinical Studies for Sickle Cell Disease Gene Therapy Using Bone Marrow CD34+ Cells Modified with a βAS3-Globin Lentiviral Vector
2011
Blood
Fabrizia Urbinati
Zulema Romero-Garcia
Sabine Geiger
Rafael Ruiz de Assin
Gabriela Kuftinec
Roger P. Hollis
Satiro N. De Oliveira
Jennifer Wherley
Aaron R. Cooper
Tim M. Townes
Elizabeth J. Read
Mark C. Walters
Herbert J. Meiselman
Thomas D. Coates
Victor J. Marder
Donald B. Kohn
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