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Veronica Verdile
Veronica Verdile
Indiana University
rna targeting
Alternative splicing
Neuromuscular disease
MRNA metabolism
Oligonucleotide
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RNA targeting in inherited neuromuscular disorders: Novel therapeutic strategies to counteract mis-splicing
2021
Cells
Veronica Verdile
Gloria Guizzo
Gabriele Ferrante
Maria Paola Paronetto
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