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Maria Luisa Jaén
Maria Luisa Jaén
Autonomous University of Barcelona
Genetic enhancement
Insulin
Glucokinase
Biology
Hormone
4
Papers
16
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0
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Seven-year follow-up of durability and safety of AAV CNS gene therapy for a lysosomal storage disorder in a large animal
2021
Molecular therapy. Methods & clinical development
Sara Marcó
Virginia Haurigot
Maria Luisa Jaén
Albert Ribera
Victor Sanchez
Maria Molas
Miguel García
Xavier León
Carles Roca
Xavier Sanchez
Joan Bertolin
Jennifer Pérez
Gemma Elias
Marc Navarro
Ana Carretero
Martí Pumarola
Anna Andaluz
Yvonne Espada
Sònia Añor
Fatima Bosch
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Treatment of skeletal and non-skeletal alterations of Mucopolysaccharidosis type IVA by AAV-mediated gene therapy.
2021
Nature Communications
Joan Bertolin
Victor Sanchez
Albert Ribera
Maria Luisa Jaén
Miquel Garcia
Anna Pujol
Xavier Sanchez
Sergio Muñoz
Sara Marcó
Jennifer Pérez
Gemma Elias
Xavier León
Carles Roca
Veronica Jimenez
Pedro J. Otaegui
Francisca Mulero
Marc Navarro
Jesús Ruberte
Fatima Bosch
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Long-Term Efficacy and Safety of Insulin and Glucokinase Gene Therapy for Diabetes: 8-Year Follow-Up in Dogs
2017
Molecular therapy. Methods & clinical development
Maria Luisa Jaén
Laia Vilà
Ivet Elias
Veronica Jimenez
Jordi Rodó
Luca Maggioni
Rafael Ruiz de Gopegui
Miguel Garcia
Sergio Muñoz
David Callejas
Eduard Ayuso
Tura Ferre
Iris Grifoll
Anna Andaluz
Jesús Ruberte
Virginia Haurigot
Fatima Bosch
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Citations (16)
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