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Guillem Pina
Guillem Pina
Disease
Tolerability
Internal medicine
Pharmacodynamics
Oral administration
2
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3
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The brain penetrant PPARγ agonist leriglitazone restores multiple altered pathways in models of X-linked adrenoleukodystrophy.
2021
Science Translational Medicine
Laura Rodríguez-Pascau
Anna Vilalta
Marc Cerrada
Estefania Traver
Sonja Forss-Petter
Isabelle Weinhofer
Jan Bauer
Stephan Kemp
Guillem Pina
Silvia Pascual
Uwe Meya
Patricia L. Musolino
Johannes Berger
Marc Martinell
Pilar Pizcueta
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A Phase 1 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Effects on Biomarkers of MIN-102 (Leriglitazone) (4149)
2020
Neurology
Uwe Meya
Guillem Pina
Silvia Pascual
Marc Cerrada-Gimenez
Pilar Pizcueta
Marc Martinell
David Eckland
Jeroen v.d. Wetering de Rooij
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