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A. Laporte
A. Laporte
Ohio State University
Spinal muscular atrophy
Genetics
Biology
SMA*
Motor neuron
2
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O.7 Spinal muscular atrophy: How it works and therapeutic targets
2013
Neuromuscular Disorders
Arthur H.M. Burghes
Vicki L. McGovern
Paul Porensky
D. Arnold
A. Laporte
K. Foust
C. Mitrpant
Thanh T. Le
S.D. Wilton
Brian K. Kaspar
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S.I.1 Development and preclinical evaluation of therapies for spinal muscular atrophy
2011
Neuromuscular Disorders
Arthur H.M. Burghes
K. Foust
Vicki L. McGovern
P. Poresnsky
A. Bevan
S. Duque
Thanh T. Le
Chitra C. Iyer
A. Laporte
I. Alwin
C. Mitrpant
S.D. Wilton
B. Kaspar
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