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Pauline Ng
Pauline Ng
GlaxoSmithKline
Endocrinology
Immunodeficiency
Biology
Strimvelis
Oncology
2
Papers
23
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Gene therapy in rare diseases: the benefits and challenges of developing a patient-centric registry for Strimvelis in ADA-SCID
2018
Orphanet Journal of Rare Diseases
Heide A. Stirnadel-Farrant
Mahesh Kudari
Nadia Garman
Jessica Imrie
Bikramjit Chopra
Stefania Giannelli
Michela Gabaldo
Ambra Corti
Stefano Zancan
Alessandro Aiuti
Maria Pia Cicalese
Rohit Batta
Jonathan Appleby
Mario Davinelli
Pauline Ng
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Citations (22)
The Management of Reflux in Infants
2012
Innovait
Nadeem Hasan
Pauline Ng
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Citations (1)
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