RNA-Based Therapies for Neurodegenerative Diseases.
2021
Most neurodegenerative disorders afflict the ageing population and are often incurable. Therefore, therapeutic development is a major focus in biomedical research. We highlight a new class of drugs, RNA molecules, to control gene expression and decrease neurotoxicity. Their efficacy is shown in pre-clinical studies, clinical trials and in cases of approved patient treatment. As the number of RNA-based strategies increases, so does the promise of targeting more disease-associated genes through a variety of different mechanisms.
- Correction
- Source
- Cite
- Save
- Machine Reading By IdeaReader
39
References
0
Citations
NaN
KQI