Enzyme reconstitution/replacement therapy for lysosomal storage diseases.
2007
Purpose of reviewOver the past 15 years, the lysosomal storage diseases have become paradigms for the specific treatment of monogenic disorders, particularly those affecting children. This review summarizes the phenotypes and recent literature regarding enzyme reconstitution (replacement) therapy an
Keywords:
- Correction
- Source
- Cite
- Save
- Machine Reading By IdeaReader
48
References
49
Citations
NaN
KQI