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Enzyme replacement therapy carries for 4-7 years in Fabry disease thereafter quality of life decreases
Enzyme replacement therapy carries for 4-7 years in Fabry disease thereafter quality of life decreases
2016
I. Ilkka Kantola
Antti-Pekka Annala
Tiina Heliö
Aki Hietaharju
Kristiina Kananen
Taru Kantola
Anne Karhu
Johanna Kuusisto
Miia Rainto
Jukka T. Saarinen
Lorenzo Sandini
Markku J. Savolainen
Jyrki Taurio
Pentti J. Tienari
Susanne Walls
Kati Valtola
Keywords:
Fabry disease
Biology
Diabetes mellitus
Enzyme replacement therapy
Genetics
Quality of life
Pediatrics
Correction
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