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592: Molecular and functional correction of a deep intronic splicing mutation in CFTR by CRISPR/Cas9 gene editing
592: Molecular and functional correction of a deep intronic splicing mutation in CFTR by CRISPR/Cas9 gene editing
2021
Stephen L. Hart
Amy Walker
M Woodall
R Maeshima
D J Pearce
M. O’Hara-Wright
David J. Sanz
I. Guerrini
A. Aldossary
Christopher OCallaghan
Deborah L. Baines
R McAnulty
Patrick T. Harrison
Keywords:
CRISPR
Medicine
Genetics
Cystic fibrosis
RNA splicing
Mutation (genetic algorithm)
Genome editing
Correction
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