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Intracorneal sequential dosing of AAV-ArsB clears corneal opacity associated with mucopolysaccharidosis VI in a feline model
Intracorneal sequential dosing of AAV-ArsB clears corneal opacity associated with mucopolysaccharidosis VI in a feline model
2021
Brian C. Gilger
Jacklyn H. Salmon
Darby Roberts
Liujiang Song
Jacquelyn J. Bower
Matthew L. Hirsch
Keywords:
Mucopolysaccharidosis VI
Ophthalmology
Dosing
Corneal opacity
Medicine
Correction
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