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Self-Inactivating Lentiviral Vectors for Correction of Rag1 Severe Combined Immunodeficiency
Self-Inactivating Lentiviral Vectors for Correction of Rag1 Severe Combined Immunodeficiency
2012
K Pike-Overzet
Mark Rodijk
Yuk Yin Ng
Mrm Baert
Chantal Lagresle-Peyrou
Axel Schambach
Fang Zhang
Rob C. Hoeben
Salima Hacein-Bey-Abina
Ac Lankester
R G M Bredius
Gja Driessen
Aj Thrasher
Christopher Baum
Marina Cavazzana-Calvo
Jjm van Dongen
F J T Staal
Keywords:
Virology
Biotechnology
Severe combined immunodeficiency
Medicine
Recombination-activating gene
Physiology
Correction
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