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First-in-human AAV Gene Therapy for Tay-Sachs Disease
First-in-human AAV Gene Therapy for Tay-Sachs Disease
2021
Miguel Sena-Esteves
Terence R. Flotte
Oguz Cataltepe
Ajit S. Puri
Ana Rita Batista
Richard P. Moser
Diane McKenna-Yasek
Catherine Douthwright
Gwladys Gernoux
Meghan Blackwood
Christian Mueller
Xuntian Jiang
Scot Bateman
Spiro Spanakis
Julia Parzych
Allison M. Keeler
Aly Abayazeed
Saurabh Rohatgi
Laura Gibson
Robert W. Finberg
Bruce A. Barton
Z Vardar
Mohammed Salman Shazeeb
Matthew J. Gounis
Florian Eichler
Robert H. Brown
Douglas R. Martin
Heather L. Gray-Edwards
Keywords:
Tay-Sachs disease
Genetic enhancement
first in human
Virology
Medicine
Correction
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