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Improved Gene Therapy for Metachromatic Leukodystrophy
Improved Gene Therapy for Metachromatic Leukodystrophy
2021
Lucas Tricoli
Adeline Vanderver
Laura Adang
Maxwell Chappell
Laura Breda
Naoto Tanaka
Michael Triebwasser
David A. Wenger
Danuta Jarocha
Amaliris Guerra
Lars Schlotawa
Karthikeyan Radhakrishnan
Rebecca C. Ahrens-Nicklas
Peter Kurre
Stephanie N Hurwitz
Stefano Rivella
Keywords:
Genetic enhancement
Metachromatic leukodystrophy
Pathology
Medicine
Correction
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