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Rescue and Phenotypic Correction in Argininosuccinate Lyase-Deficient Mice by AAV8.ASL Transfer
Rescue and Phenotypic Correction in Argininosuccinate Lyase-Deficient Mice by AAV8.ASL Transfer
2017
Julien Baruteau
D Perocheau
Joanna Hanley
Eridan Rocha-Ferreira
R Karda
J Ng
Ahad A. Rahim
N Suff
Blerida Banushi
Helen Prunty
Mariya Hristova
Simon Heales
Steven J. Howe
Smk Buckley
Philippa B. Mills
Paul Gissen
Simon N. Waddington
Keywords:
Argininosuccinate lyase
Molecular biology
Biotechnology
Phenotype
Medicine
Physiology
deficient mouse
Correction
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