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Year 2 results for a phase 3 trial of voretigene neparvovec in biallelic RPE65-mediated inherited retinal disease
Year 2 results for a phase 3 trial of voretigene neparvovec in biallelic RPE65-mediated inherited retinal disease
2017
Stephen R. Russell
Jean Bennett
Jennifer Wellman
Daniel C. Chung
Katherine A. High
Zi-Fan Yu
Amy Tillman
Albert M. Maguire
Keywords:
Anatomy
Diabetes mellitus
Disease
Genetics
RPE65
Retinal
Biology
Bioinformatics
Correction
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