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Martha L. Solano
Martha L. Solano
Medicine
Enzyme replacement therapy
Pediatrics
Sanfilippo syndrome
Lysosomal storage disorders
5
Papers
7
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0
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2024
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Natural history of Sanfilippo syndrome type B in young patients: Ongoing results from two large, prospective studies
2021
Molecular Genetics and Metabolism
Roberto Giugliani
İlyas Okur
Fatih Süheyl Ezgü
Nicole Muschol
Paul Harmatz
María José de Castro-López
María L. Couce
Shuan-Pei Lin
Spyros Batzios
Maureen Cleary
Martha L. Solano
Hernán Amartino
Heidi Peters
Joy Lee
Joseph Kovalchin
Eric Zanelli
Stephen M. Maricich
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Mucopolisacaridosis: generalidades y compromiso cardiovascular
2021
Revista Colombiana de Cardiología
Claudia Stapper
Martha L. Solano
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Tralesinidase alfa (AX 250) enzyme replacement therapy for Sanfilippo syndrome type B
2021
Molecular Genetics and Metabolism
Nicole Muschol
Katharina von Cossel
İlyas Okur
Fatih Süheyl Ezgü
María José de Castro-López
María L. Couce
Paul Harmatz
Spyros Batzios
Maureen Cleary
Martha L. Solano
Shaun Pei Lin
Roberto Giugliani
Hernán Amartino
Heidi Peters
Joy Lee
Joseph Kovalchin
Eric Zanelli
Stephen M. Maricich
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Development of a Clinical Algorithm for the Early Diagnosis of Mucopolysaccharidosis III
2020
Maria L. Escolar
Jessica Bradshaw
Valerie Tharp Byers
Roberto Giugliani
Lynn Golightly
Charles Marques Lourenço
Kimberly McDonald
Nicole Muschol
Imogen Newsom-Davis
Cara ONeill
Holly L. Peay
Jennifer Siedman
Martha L. Solano
Tessa Wirt
Tim Wood
Lonnie Zwaigenbaum
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Enzyme replacement therapy interruption in patients with Mucopolysaccharidoses: Recommendations for distinct scenarios in Latin America
2020
Molecular genetics and metabolism reports
Martha L. Solano
Alejandro Fainboim
Juan Politei
Gloria Liliana Porras Hurtado
Ana Maria Martins
Carolina Fischinger Moura de Souza
Felipe Mendez Koch
Hernán Amartino
José María Satizábal
Dafne Dain Gandelman Horovitz
Paula Frassinetti Vasconcelos de Medeiros
Rachel Sayuri Honjo
Charles Marques Lourenço
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Citations (7)
1