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Simone A. Haas
Simone A. Haas
University of Freiburg
Genome editing
Transcription activator-like effector nuclease
Medicine
Gene
Immune system
3
Papers
6
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0
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A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa.
2021
Molecular therapy. Nucleic acids
Thomas Kocher
Johannes Bischof
Simone A. Haas
Oliver Patrick March
Bernadette Liemberger
Stefan Hainzl
Julia Illmer
Anna Hoog
Katharina Muigg
Heide-Marie Binder
Alfred Klausegger
Dirk Strunk
Johann W Bauer
Toni Cathomen
Ulrich Koller
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Citations (1)
Automated generation of gene-edited CAR T cells at clinical scale
2020
Molecular therapy. Methods & clinical development
Jamal Alzubi
Dominik Lock
Manuel Rhiel
Sabrina Schmitz
Stefan Wild
Claudio Mussolino
Markus Hildenbeutel
Caroline Brandes
Julia Rositzka
Simon Lennartz
Simone A. Haas
Kay O. Chmielewski
Thomas Schaser
Andrew Kaiser
Toni Cathomen
Tatjana I. Cornu
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Citations (5)
A Highly Efficient and GMP Compliant Protocol to Manufacture CCR5 Edited Cells to Treat HIV Infection
2018
Blood
Marianna Romito
Emily Meyer
Sushmita Poddar
Helena Heinz
Julia Rositzka
Markus Hildenbeutel
Anne-Sophie Gautron
Brian W. Busser
Yik Lim Kok
Giandomenico Turchiano
Simone A. Haas
Richard Schäfer
Julianne Smith
Karin J. Metzner
Claudio Mussolino
Philippe Duchateau
Toni Cathomen
Tatjana I. Cornu
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