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Julia Johansson
Julia Johansson
University of Pennsylvania
Cerebrospinal fluid
Central nervous system
Genetic enhancement
Medicine
Spinal muscular atrophy
2
Papers
11
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Translational feasibility of lumbar puncture for intrathecal AAV administration
2020
Molecular therapy. Methods & clinical development
Christian Hinderer
Nathan Katz
Cecilia Dyer
Tamara Goode
Julia Johansson
Peter Bell
Laura K. Richman
Elizabeth L. Buza
James M. Wilson
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Citations (6)
Adeno-associated virus serotype 1-based gene therapy for FTD caused by GRN mutations.
2020
Annals of clinical and translational neurology
Christian Hinderer
Rod Miller
Cecilia Dyer
Julia Johansson
Peter Bell
Elizabeth L. Buza
James M. Wilson
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Citations (5)
1