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G. Amini Chermahini
G. Amini Chermahini
Genetics
Biology
DUX4
Diabetes mellitus
Bioinformatics
3
Papers
1
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0
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O.8DUX4 mRNA silencing with CRISPR-Cas13 gene therapy as a prospective treatment for Facioscapulohumeral muscular dystrophy
2019
Neuromuscular Disorders
Afrooz Rashnonejad
G. Amini Chermahini
Lindsay M. Wallace
Scott Q. Harper
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P.50An in situ hybridization-based method for detecting DUX4 RNA expression in vitro
2019
Neuromuscular Disorders
G. Amini Chermahini
Afrooz Rashnonejad
Scott Q. Harper
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P.49Translating DUX4-targeted RNAi-based gene therapy for FSHD
2019
Neuromuscular Disorders
Lindsay M. Wallace
G. Amini Chermahini
Allison M. Fowler
M. Guggenbiller
K. Kazimir
C. Cash
S. Knoblaugh
Scott Q. Harper
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