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Alex J. Harvey
Alex J. Harvey
Recombinant DNA
Lysosomal acid lipase deficiency
Lysosomal Acid Lipase
Enzyme replacement therapy
Diabetes mellitus
2
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6
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Enzyme lysosomal storage disease
2011
Anthony G. Quinn
Alex J. Harvey
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SBC-102, a recombinant enzyme replacement therapy corrects clinically relevant phenotypic abnormalities in a rat model of lysosomal acid lipase deficiency
2011
Molecular Genetics and Metabolism
Anthony G. Quinn
Mark Leavitt
Wei Hu
Alex J. Harvey
Michael Chen
Tamas Nagy
Angela Lents
Emelie Balmes
Sara Mathews
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Citations (6)
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