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P1213 : Adeno-associated virus vector-mediated liver gene therapy for Crigler-Najjar syndrome
P1213 : Adeno-associated virus vector-mediated liver gene therapy for Crigler-Najjar syndrome
2015
Piter J. Bosma
P. Labrune
N. Brunetti-Pierri
L. D’Antiga
Michael Ott
M. Beinat
F. Ronchi
Fulvio Mavilio
U. Beuers
Andrés F. Muro
Ulrich Baumann
F. Mingozzi
Keywords:
Adeno-associated virus
Virology
Crigler–Najjar syndrome
Medicine
Genetic enhancement
Diabetes mellitus
Correction
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