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Muna El-Khairi
Muna El-Khairi
Medicine
Spinal muscular atrophy
SMA*
Pathology
Neuromuscular disease
5
Papers
55
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Risdiplam in Type 1 Spinal Muscular Atrophy.
2021
The New England Journal of Medicine
Giovanni Baranello
Basil T. Darras
John W. Day
Nicolas Deconinck
Andrea Klein
Riccardo Masson
Eugenio Mercuri
Kristy J. Rose
Muna El-Khairi
Marianne Gerber
Ksenija Gorni
Omar Khwaja
Heidemarie Kletzl
Renata S. Scalco
Timothy Seabrook
Paulo Fontoura
Laurent Servais
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Citations (44)
Risdiplam-Treated Infants with Type 1 Spinal Muscular Atrophy versus Historical Controls
2021
The New England Journal of Medicine
Basil T. Darras
Riccardo Masson
Maria Mazurkiewicz-Bełdzińska
Kristy Rose
Hui Xiong
Edmar Zanoteli
Giovanni Baranello
Claudio Bruno
D. Vlodavets
Yi Wang
Muna El-Khairi
Marianne Gerber
Ksenija Gorni
Omar Khwaja
Heidemarie Kletzl
Renata S. Scalco
Paulo Fontoura
Laurent Servais
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Citations (7)
FIREFISH Parts 1 and 2: 12-month pooled safety and efficacy outcomes of risdiplam (RG7916) in infants with Type 1 spinal muscular atrophy (SMA)
2020
Neuromuscular Disorders
L. Servais
O. Bloespflug-Tanguy
Basil T. Darras
John C. Day
Nicolas Deconinck
Andrea Klein
Riccardo Masson
M. Mazurkiewicz-Beldzinska
E. Mercuri
Kristy Rose
D. Vlodavets
Hui Xiong
Edmar Zanoteli
A Dodman
Muna El-Khairi
M. Gerber
Ksenija Gorni
Heidemarie Kletzl
Renata S. Scalco
Giovanni Baranello
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FIREFISH Part 2: Efficacy and safety of risdiplam (RG7916) in infants with Type 1 spinal muscular atrophy (SMA)
2020
European Respiratory Journal
Giovanni Baranello
Laurent Servais
Riccardo Masson
Maria Mazurkiewicz-Bełdzińska
Kristy J. Rose
D. Vlodavets
Hui Xiong
Edmar Zanoteli
Muna El-Khairi
Sabine Fuerst-Recktenwald
Marianne Gerber
Ksenija Gorni
Heidemarie Kletzl
Renata S. Scalco
Basil T. Darras
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Citations (4)
Mathematical modelling of tuberculosis infection
2013
Muna El-Khairi
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