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A Dodman
A Dodman
SMA*
Medicine
Spinal muscular atrophy
Slope stability
Banded iron formation
4
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FIREFISH Parts 1 and 2: 24-Month Safety and Efficacy of Risdiplam in Type 1 SMA
2021
R. Masson
Odile Boespflug-Tanguy
Basil T. Darras
John W. Day
Nicolas Deconinck
Andrea Klein
M. Mazurkiewicz-Bedziska
Eugenio Mercuri
Kristy Rose
L. Servais
D. Vlodavets
H. Xiong
Edmar Zanoteli
A Dodman
M. El-Khairi
E. Gaki
Marianne Gerber
Ksenija Gorni
Heidemarie Kletzl
G. Baranello
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IREFISH Parts 1 and 2: 24-month safety and efficacy of risdiplam in type 1 spinal muscular atrophy (SMA)
2021
Neuromuscular Disorders
Riccardo Masson
Odile Boespflug-Tanguy
Basil T. Darras
J. Day
Nicolas Deconinck
Andrea Klein
Maria Mazurkiewicz-Bełdzińska
Eugenio Mercuri
Kristy Rose
L. Servais
D. Vlodavets
H. Xiong
Edmar Zanoteli
A Dodman
M. El-Khairi
E. Gaki
Marianne Gerber
Ksenija Gorni
Heidemarie Kletzl
Giovanni Baranello
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FIREFISH Parts 1 and 2: 12-month pooled safety and efficacy outcomes of risdiplam (RG7916) in infants with Type 1 spinal muscular atrophy (SMA)
2020
Neuromuscular Disorders
L. Servais
O. Bloespflug-Tanguy
Basil T. Darras
John C. Day
Nicolas Deconinck
Andrea Klein
Riccardo Masson
M. Mazurkiewicz-Beldzinska
E. Mercuri
Kristy Rose
D. Vlodavets
Hui Xiong
Edmar Zanoteli
A Dodman
Muna El-Khairi
M. Gerber
Ksenija Gorni
Heidemarie Kletzl
Renata S. Scalco
Giovanni Baranello
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Pit slope depressurisation investigation for an open cut iron ore mine in the Pilbara
2013
A Dodman
G. Beale
J Rodríguez
A. Cottrell
J. Youngs
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